Three women who received life-saving heart transplants have donated their own diseased hearts to medical research, with the organs now…
Browsing: Gene Therapy
Millions of people carry a hidden form of bad cholesterol that is not picked up by standard blood tests and,…
‘I’m watching my child fade away every single day, and it’s enough to break a person,’ says Georgia Nonas, 29.…
The US Food and Drug Administration was thrown into fresh turmoil on Friday after its top drug and vaccine chiefs…
Reed Jobs, the 34-year-old son of Apple co-founder Steve Jobs, has turned the trauma of watching his father die from…
Hundreds more children with spinal muscular atrophy (SMA) can now access life-changing NHS treatments after the National Institute for Health…
England will screen 750,000 newborns for spinal muscular atrophy as part of a landmark study to determine whether the genetic…
A six-year-old girl from Hertfordshire has had her sight restored by a pioneering gene therapy on the NHS, a treatment…
Two young brothers from west London are in a race against time to find the stem cell donors who could…
The national rollout of screening for the rare genetic condition spinal muscular atrophy (SMA) in newborns is to begin earlier…